Orchard Therapeutics Gains First U.S. Approval for a Metachromatic Leukodystrophy Gene Therapy
Human Gene Therapy,Volume 35, Issue 7-8, Page 215-218, April 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 16, 2024 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Remembrances of Kenneth Berns, PhD
Human Gene Therapy,Volume 35, Issue 7-8, Page 203-214, April 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 16, 2024 Category: Genetics & Stem Cells Source Type: research
Role of FoxP3+ Regulatory T Cells in Modulating Immune Responses to Adeno-Associated Virus Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 11, 2024 Category: Genetics & Stem Cells Authors: Maite Mu ñoz-Melero Moanaro Biswas Source Type: research
A Review of the Cost-Effectiveness Evidence for FDA-Approved Cell and Gene Therapies
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 9, 2024 Category: Genetics & Stem Cells Authors: Sumaya Abuloha Shu Niu Darlene Adirika Benjamin P. Harvey Mikael Svensson Source Type: research
Development of AAV-Mediated Gene Therapy Approaches to Treat Skeletal Diseases
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - April 8, 2024 Category: Genetics & Stem Cells Authors: Chujiao Lin Matthew B. Greenblatt Guangping Gao Jae-Hyuck Shim Source Type: research
Pre-Existing Immunity to a Nucleic Acid Contaminant-Derived Antigen Mediates Transaminitis and Resultant Diminished Transgene Expression in a Mouse Model of Hepatic Recombinant Adeno-Associated Virus-Mediated Gene Transfer
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 28, 2024 Category: Genetics & Stem Cells Authors: Mark A. Brimble Christopher L. Morton Stephen M. Winston Isaiah L. Reeves Yunyu Spence Pei-Hsin Cheng Junfang Zhou Amit C. Nathwani Paul G. Thomas Aisha Souquette Andrew M. Davidoff Source Type: research
Correction to: Efficacy and Safety of Adeno-Associated Virus-Based Clinical Gene Therapy for Hemophilia: A Systematic Review and Meta-Analysis, by Han et al. Hum Gene Ther 2024;35(3-4):93 –103; doi: 10.1089/hum.2023.208.
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 25, 2024 Category: Genetics & Stem Cells Source Type: research
Complement System Response to Adeno-Associated Virus Vector Gene Therapy
Human Gene Therapy, Ahead of Print. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 18, 2024 Category: Genetics & Stem Cells Authors: Elizabeth Kropf David M. Markusic Anna Majowicz Federico Mingozzi Klaudia Kuranda Source Type: research
Therapeutic Strategy for Fabry Disease by Intravenous Administration of Adeno-Associated Virus 9 in a Symptomatic Mouse Model
Human Gene Therapy,Volume 35, Issue 5-6, Page 192-201, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Yuka Hayashi Yoshihide Sehara Ryota Watano Kenji Ohba Yuki Takayanagi Yoshio Sakiyama Kazuhiro Muramatsu Hiroaki Mizukami Source Type: research
Combination Immunotherapy of Oncolytic Flu-Vectored Virus and Programmed Cell Death 1 Blockade Enhances Antitumor Activity in Hepatocellular Carcinoma
Human Gene Therapy,Volume 35, Issue 5-6, Page 177-191, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Hongyu Yu Fang Sun Yan Xu Hao Yang Chongyu Tian Cong Li Yimin Kang Lei Hao Penghui Yang Source Type: research
Gutless Helper-Dependent and First-Generation HAdV5 Vectors Have Similar Mechanical Properties and Common Transduction Mechanisms
Human Gene Therapy,Volume 35, Issue 5-6, Page 163-176, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Lars Thalmann Natalia Martin-Gonzalez Dominik Br ücher Andreas Pl ückthun Pedro J. de Pablo Maarit Suomalainen Urs F. Greber Source Type: research
Knockout and Replacement Gene Surgery to Treat Rhodopsin-Mediated Autosomal Dominant Retinitis Pigmentosa
Human Gene Therapy,Volume 35, Issue 5-6, Page 151-162, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Xuehan Sun Chen Liang Yangcan Chen Tongtong Cui Jiabao Han Moyu Dai Ying Zhang Qi Zhou Wei Li Source Type: research
Current Status and Prospects of Viral Vector-Based Gene Therapy to Treat Kidney Diseases
Human Gene Therapy,Volume 35, Issue 5-6, Page 139-150, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Louise Medaer Koenraad Veys Rik Gijsbers Source Type: research
Akouos Therapy Restores 11-Year-Old Boy's Hearing After 1 Month
Human Gene Therapy,Volume 35, Issue 5-6, Page 135-138, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Alex Philippidis Source Type: research
Kenneth I. Berns, MD, PhD [1938 –2024]
Human Gene Therapy,Volume 35, Issue 5-6, Page 133-134, March 2024. (Source: Human Gene Therapy)
Source: Human Gene Therapy - March 14, 2024 Category: Genetics & Stem Cells Authors: Barry J. Byrne Terence R. Flotte Roland W. Herzog Arun Srivastava Source Type: research
